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Articles Tagged with SMA phenotype

Race for a Cure

An interview with Christian Lorson, Associate Professor of Veterinary Medicine

Spinal Muscular Atrophy (SMA) is the leading genetic cause of infantile death and the leading genetic killer of children under the age of two. As an associate professor in MU’s Department of Veterinary Pathobiology, Christian Lorson has dedicated his life’s research to the study of this devastating disease in hopes of someday developing therapies to replace the diseased gene with a ‘healthy” one.

Audio and Video Tagged with SMA phenotype

Looking Forward

From an interview with Christian Lorson, Associate Professor of Veterinary Medicine

With research under his belt, Lorson hopes that his team can start to establish clinical trials to test the therapeutic programs they have developed. “The next step is to launch it into animal models and prove efficacy, showing that you can turn around the SMA phenotype [gene expression].”